Immunodeficiencies
18
4
6
8
Key Insights
Highlights
Success Rate
80% trial completion
Clinical Risk Assessment
Based on trial outcomes
High Risk
Score: 59/100
11.1%
2 terminated out of 18 trials
80.0%
-6.5% vs benchmark
6%
1 trials in Phase 3/4
63%
5 of 8 completed with results
Key Signals
Data Visualizations
Phase Distribution
Trial Status
Trial Success Rate
Benchmark: 86.5%
Based on 8 completed trials
Clinical Trials (18)
Reduced Intensity Conditioning (RIC) Regimen for Patients With Non-malignant Disorders
Studies of the Pathogenesis of HIV Infection in Human Peripheral Blood Cells and/or Body Fluids in People Living With and Without HIV
Expanded Access Protocol Using CD3+/CD19+ Depleted PBSC
V-IMMUNE: A Novel Immunoglobulin Therapy for Immunodeficiency
Alpha/Beta T and CD19+ Depleted Peripheral Stem Cells for Patients With Primary Immunodeficiencies
Second or Greater Allogeneic Hematopoietic Stem Cell Transplant Using Reduced Intensity Conditioning (RIC)
Expanded Access Protocol Using Alpha/Beta T and CD19+ Depleted PBSC
CHP 834 Unrelated and Partially Matched Related Donor Peripheral Stem Cell Transportation for T and B Cell Depletion
COVID-19 Vaccination and Outcomes in Individuals With and Without Immune Deficiencies and Dysregulations
Study of Fludarabine Drug Exposure in Pediatric Bone Marrow Transplantation
Study of Clofarabine and Fludarabine Drug Exposure in Pediatric Bone Marrow Transplantation (HCT)
Study of Melphalan Drug Exposure in Pediatric Hematopoietic Stem Cell Transplant Patients
Double Cord Blood Transplant for Patients With Malignant and Non-malignant Disorders
CD34+Selection for Partially Matched Family or Matched Unrelated Adult Donor Transplant
Reduced Intensity Conditioning Using CD3+/CD19+ Depletion for Non Malignant Transplantable Diseases
Novel Testing Procedures
Unrelated Donor Transplant for Malignant and Non-Malignant Disorders
Reduced Intensity Conditioning for Umbilical Cord Blood Transplant in Pediatric Patients With Non-Malignant Disorders