Hereditary Motor and Sensory Neuropathies
2
0
1
1
Key Insights
Highlights
Success Rate
100% trial completion (above average)
Treatment Research
2 treatments under study, led by Ascorbic Acid
Related Conditions
Often studied with 13 related conditions
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 50/100
0.0%
0 terminated out of 2 trials
100.0%
+13.4% vs benchmark
0%
0 trials in Phase 3/4
0%
0 of 1 completed with results
Key Signals
Data Visualizations
Phase Distribution
Trial Status
Trial Success Rate
Benchmark: 86.6%
Based on 1 completed trials
Clinical Trials (2)
Research Network
Common Treatments
- Ascorbic Acid1
- Assistive Gait Devices Combined With Physiotherapy1
Active Sponsors
- LMU Klinikum1
- Academisch Medisch Centrum - Universiteit van Amsterdam (AMC-UvA)1
Top Investigators
Department of Neurology, Academic Medical Center, University of Amsterdam
Department of Neurology, Academic Medical Center, University of Amsterdam
Department of Neurology, Academic Medical Center, University of Amsterdam
Department of Neurology, Academic Medical Center, University of Amsterdam
Department of Neurology, Academic Medical Center, University of Amsterdam
Related Conditions
- Limb Girdle Muscular Dystrophies1
- Friedreich Ataxia1
- Guillain Barré Syndrome1
- Inclusion Body Myositis1
- Charcotmarietooth Disease1