Key Insights

Highlights

Success Rate

100% trial completion (above average)

Treatment Research

2 treatments under study, led by Ascorbic Acid

Related Conditions

Often studied with 13 related conditions

Clinical Risk Assessment

Based on trial outcomes

Moderate Risk

Score: 50/100

Termination Rate

0.0%

0 terminated out of 2 trials

Success Rate

100.0%

+13.4% vs benchmark

Late-Stage Pipeline

0%

0 trials in Phase 3/4

Results Transparency

0%

0 of 1 completed with results

Key Signals

100% success

Data Visualizations

Phase Distribution

2Total
Not Applicable (1)
Phase 2 (1)

Trial Status

Completed1
Enrolling By Invitation1

Trial Success Rate

100.0%

Benchmark: 86.6%

Based on 1 completed trials

Clinical Trials (2)

Research Network

Common Treatments

  • Ascorbic Acid1
  • Assistive Gait Devices Combined With Physiotherapy1

Active Sponsors

  • LMU Klinikum1
  • Academisch Medisch Centrum - Universiteit van Amsterdam (AMC-UvA)1

Top Investigators

Related Conditions

  • Limb Girdle Muscular Dystrophies1
  • Friedreich Ataxia1
  • Guillain Barré Syndrome1
  • Inclusion Body Myositis1
  • Charcotmarietooth Disease1

Activity Timeline