Key Insights

Highlights

Success Rate

96% trial completion (above average)

Clinical Risk Assessment

Based on trial outcomes

Moderate Risk

Score: 40/100

Termination Rate

2.4%

1 terminated out of 41 trials

Success Rate

96.3%

+9.8% vs benchmark

Late-Stage Pipeline

12%

5 trials in Phase 3/4

Results Transparency

15%

4 of 26 completed with results

Key Signals

4 with results96% success

Data Visualizations

Phase Distribution

27Total
Not Applicable (5)
P 1 (6)
P 2 (11)
P 3 (4)
P 4 (1)

Trial Status

Completed26
Unknown5
Recruiting4
Active Not Recruiting3
Enrolling By Invitation1
Not Yet Recruiting1

Trial Success Rate

96.3%

Benchmark: 86.5%

Based on 26 completed trials

Clinical Trials (41)

Showing 20 of 20 trials
NCT04404881Phase 2Active Not RecruitingPrimary

Bevacizumab In Hereditary Hemorrhagic Telangiectasia

NCT06659640Phase 1RecruitingPrimary

A Study to Evaluate ALN-6400 in Healthy Volunteers and Patients With Hereditary Hemorrhagic Telangiectasia (HHT)

NCT04874558CompletedPrimary

Ultra-low-dose Chest CT for HHT

NCT04150822Active Not RecruitingPrimary

CHORUS - Comprehensive HHT Outcomes Registry of the United States (Formerly OUR HHT Registry)

NCT01158807CompletedPrimary

Cerebral Hemorrhage Risk in Hereditary Hemorrhagic Telangiectasia

NCT03850964Phase 2Active Not RecruitingPrimary

Effects of Pazopanib on Hereditary Hemorrhagic Telangiectasia Related Epistaxis and Anemia (Paz)

NCT05954481Not ApplicableCompletedPrimary

Stress-Echography in Hereditary Haemorrhagic Telangiectasia Patient With Hepatic Involvement

NCT07101575Not Yet RecruitingPrimary

Cardiac Evaluation in Hereditary Hemorrhagic Telangiectasia

NCT06259292RecruitingPrimary

Comprehensive HHT Outcomes Registry of the United States (CHORUS)

NCT05641142Not ApplicableRecruitingPrimary

Prospective Study of Antiplatelet and Anticoagulation Therapy in Hereditary Haemorrhagic Telangiectasia

NCT04646356Phase 2CompletedPrimary

Tacrolimus Trial for Hereditary Hemorrhagic Telangiectasia (HHT)

NCT06261333Enrolling By InvitationPrimary

Quality of Life in Patients With Hemorrhagic Telangiectasia

NCT05550376CompletedPrimary

Genotype-phenotype Association in Hereditary Hemorrhagic Telangiectasia

NCT05269849Phase 2CompletedPrimary

Sirolimus for Nosebleeds in HHT

NCT04469517RecruitingPrimary

Influence of Hypoxic Induced Factors in Patients With Hereditary Hemorrhagic Telangiectasia

NCT01931644Completed

At-Home Research Study for Patients With Autoimmune, Inflammatory, Genetic, Hematological, Infectious, Neurological, CNS, Oncological, Respiratory, Metabolic Conditions

NCT02436213Not ApplicableCompleted

Cardiopulmonary Exercise Testing to Evaluate Pulmonary AVMs

NCT01752049Phase 1CompletedPrimary

Topical Anti-angiogenic Therapy for Telangiectasia in HHT: Proof of Concept

NCT05752253Not ApplicableCompletedPrimary

Counseling Intervention in Hereditary Hemorrhagic Telangiectasia in the COVID Era.

NCT03850730Phase 1UnknownPrimary

Pazopanib for the Treatment of Epistaxis in Hereditary Hemorrhagic Telangiectasia

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