Key Insights

Highlights

Success Rate

67% trial completion

Treatment Research

11 treatments under study, led by Emicizumab

Research Leaders

18 sponsors active, led by Dutch Society of Haemophilia Patients

Related Conditions

Often studied with 9 related conditions

Clinical Risk Assessment

Based on trial outcomes

Low Risk

Score: 27/100

Termination Rate

12.5%

1 terminated out of 8 trials

Success Rate

66.7%

-19.9% vs benchmark

Late-Stage Pipeline

38%

3 trials in Phase 3/4

Results Transparency

100%

2 of 2 completed with results

Key Signals

2 with results67% success

Data Visualizations

Phase Distribution

5Total
Not Applicable (1)
Phase 1 (1)
Phase 3 (2)
Phase 4 (1)

Trial Status

Completed2
Unknown2
Recruiting1
Not Yet Recruiting1
Terminated1
Active Not Recruiting1

Trial Success Rate

66.7%

Benchmark: 86.6%

Based on 2 completed trials

Clinical Trials (8)

Research Network

Common Treatments

  • Emicizumab2
  • Homebased Exercise Intervention1
  • Kn0571
  • Emicizumab Dosis Continuation Group1
  • Emicizumab Dose Adjustment Group1

Active Sponsors

  • Dutch Society of Haemophilia Patients1
  • Amsterdam University Medical Center1
  • Oslo University Hospital1
  • Leiden University Medical Center1
  • Catalyst Biosciences1

Top Investigators

Related Conditions

  • Hemophilia A With Inhibitor3
  • Hemophilia B Without Inhibitor2
  • Hemophilia B1
  • Adult1
  • Hemophilia B With Inhibitor1

Activity Timeline