Key Insights

Highlights

Success Rate

100% trial completion (above average)

Clinical Risk Assessment

Based on trial outcomes

Moderate Risk

Score: 30/100

Termination Rate

0.0%

0 terminated out of 15 trials

Success Rate

100.0%

+13.5% vs benchmark

Late-Stage Pipeline

33%

5 trials in Phase 3/4

Results Transparency

33%

3 of 9 completed with results

Key Signals

3 with results100% success

Data Visualizations

Phase Distribution

10Total

P 2 (5)

P 3 (4)

P 4 (1)

Trial Status

Completed9

Unknown5

Active Not Recruiting1

Trial Success Rate

100.0%

Benchmark: 86.5%

Based on 9 completed trials

Clinical Trials (15)

Showing 15 of 15 trials

NCT06903234Active Not RecruitingPrimary

Post-authorization Safety Study of Iptacopan in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) Using Data From the IPIG PNH Registry

NCT00997386Phase 2Completed

Reduced Intensity Allogeneic PBSCT to Treat Hematologic Malignancies and Hematopoietic Failure States

NCT00867932Phase 4CompletedPrimary

Eculizumab Pharmacokinetics/Pharmacodynamics Study in Pediatric/Adolescent Paroxysmal Nocturnal Hemoglobinuria (PNH)

NCT00618969Phase 2Completed

Peripheral Blood Stem Cell Transplantation (PBSCT)From Haploidentical Related Donors

NCT00975975Phase 2Completed

Basiliximab #2: In-Vivo Activated T-Cell Depletion to Prevent Graft-Versus_Host Disease (GVHD) After Nonmyeloablative Allotransplantation for the Treatment of Blood Cancer

NCT00438789UnknownPrimary

The Paroxysmal Nocturnal Hemoglobinuria Early Access Treatment Protocol

NCT01760096Phase 2Unknown

Safety and Efficacy of Levamisole Combined With Cyclosporine A in Patients With Subclinical Paroxysmal Nocturnal Hemoglobinuria and PNH in the Setting of Another Bone Marrow Failure Syndromes(PNH-2013)

NCT01642979Phase 2Unknown

Safety and Efficacy of Levamisole Combined With Cyclosporine A in Patients With Classic Paroxysmal Nocturnal Hemoglobinuria

NCT00721864CompletedPrimary

The Molecular Biology of Paroxysmal Nocturnal Hemoglobinuria (PNH)

NCT01224483UnknownPrimary

Multicenter Retrospective Analysis About the Clinical Characteristics of Korean Paroxysmal Nocturnal Hemoglobinuria (PNH) Patients

NCT00315419Unknown

Identifying Characteristics of Bone Marrow Failure Syndromes

NCT00152139Phase 3Completed

Stem Cell Transplantation for Patients With Hematologic Malignancies

NCT00098280Phase 3CompletedPrimary

Eculizumab to Treat Paroxysmal Nocturnal Hemoglobinuria