Key Insights

Highlights

Treatment Research

5 treatments under study, led by Aav2haqp1 Concentration 1

Clinical Risk Assessment

Based on trial outcomes

Moderate Risk

Score: 50/100

Termination Rate

0.0%

0 terminated out of 2 trials

Late-Stage Pipeline

0%

0 trials in Phase 3/4

Results Transparency

0%

0 of 0 completed with results

Key Signals

Data Visualizations

Phase Distribution

2Total
Phase 2 (2)

Trial Status

Active Not Recruiting1
Enrolling By Invitation1

Clinical Trials (2)

Research Network

Common Treatments

  • Aav2haqp1 Concentration 11
  • Aav2haqp11
  • Aav2haqp1 Concentration 31
  • Aav2haqp1 Concentration 21
  • Aav2haqp1 Concentration 41

Active Sponsors

  • MeiraGTx, LLC2

Activity Timeline