Condition
Glycogen Storage Disease Type IV
Total Trials
4
Recruiting
1
Active
1
Completed
1
Success Rate
100.0%+13% vs avg
Key Insights
Highlights
Success Rate
100% trial completion (above average)
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 50/100
Termination Rate
0.0%
0 terminated out of 4 trials
Success Rate
100.0%
+13.5% vs benchmark
Late-Stage Pipeline
0%
0 trials in Phase 3/4
Results Transparency
0%
0 of 1 completed with results
Key Signals
100% success
Data Visualizations
Phase Distribution
2Total
Not Applicable (1)
P 2 (1)
Trial Status
Recruiting1
Withdrawn1
Completed1
Unknown1
Trial Success Rate
100.0%
Benchmark: 86.5%
Based on 1 completed trials
Clinical Trials (4)
Showing 4 of 4 trials
NCT02683512RecruitingPrimary
GBE Deficiency (GSD IV and APBD) Natural History Study
NCT02385162Withdrawn
Biomarker for Glycogen Storage Diseases (BioGlycogen)
NCT02635269Not ApplicableUnknown
Fat and Sugar Metabolism During Exercise in Patients With Metabolic Myopathy
NCT00947960Phase 2Completed
Triheptanoin Treatment Trial for Patients With Adult Polyglucosan Body Disease
Showing all 4 trials