Condition
Glycogen Storage Disease Type II Late Onset
Total Trials
2
Recruiting
0
Active
1
Completed
0
Key Insights
Highlights
Treatment Research
2 treatments under study, led by Avalglucosidase Alfa
Related Conditions
Often studied with 9 related conditions
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 30/100
Termination Rate
0.0%
0 terminated out of 2 trials
Late-Stage Pipeline
50%
1 trials in Phase 3/4
Results Transparency
0%
0 of 0 completed with results
Key Signals
Data Visualizations
Phase Distribution
2Total
Phase 2 (1)
Phase 4 (1)
Trial Status
Active Not Recruiting1
Unknown1
Clinical Trials (2)
Research Network
Common Treatments
- Avalglucosidase Alfa1
- Multiingredient Supplement Pdtmis1
Active Sponsors
- McMaster University1
- Iris Plug1
- Sanofi1
Top Investigators
Erasmus Medical Center
McMaster University
Related Conditions
- Pompe Disease2
- Lysosomal Storage Diseases1
- Nutrition Poor1
- Muscle Loss1
- Pompe Disease Lateonset1