Key Insights

Highlights

Treatment Research

2 treatments under study, led by Avalglucosidase Alfa

Related Conditions

Often studied with 9 related conditions

Clinical Risk Assessment

Based on trial outcomes

Moderate Risk

Score: 30/100

Termination Rate

0.0%

0 terminated out of 2 trials

Late-Stage Pipeline

50%

1 trials in Phase 3/4

Results Transparency

0%

0 of 0 completed with results

Key Signals

Data Visualizations

Phase Distribution

2Total
Phase 2 (1)
Phase 4 (1)

Trial Status

Active Not Recruiting1
Unknown1

Clinical Trials (2)

Research Network

Common Treatments

  • Avalglucosidase Alfa1
  • Multiingredient Supplement Pdtmis1

Active Sponsors

  • McMaster University1
  • Iris Plug1
  • Sanofi1

Top Investigators

Related Conditions

  • Pompe Disease2
  • Lysosomal Storage Diseases1
  • Nutrition Poor1
  • Muscle Loss1
  • Pompe Disease Lateonset1

Activity Timeline