Key Insights

Highlights

Treatment Research

1 treatments under study, led by Multiingredient Supplement Pdtmis

Related Conditions

Often studied with 7 related conditions

Clinical Risk Assessment

Based on trial outcomes

Moderate Risk

Score: 50/100

Termination Rate

0.0%

0 terminated out of 2 trials

Late-Stage Pipeline

0%

0 trials in Phase 3/4

Results Transparency

0%

0 of 0 completed with results

Key Signals

Data Visualizations

Phase Distribution

1Total
Phase 2 (1)

Trial Status

Recruiting1
Unknown1

Clinical Trials (2)

Showing 2 of 2 trials
NCT03564561RecruitingPrimary

Natural History of Pompe Disease

NCT06130228Phase 2Unknown

Nutritional Therapy in Late-onset Pompe Disease

Showing all 2 trials

Research Network

Common Treatments

  • Multiingredient Supplement Pdtmis1

Active Sponsors

  • Assistance Publique - Hôpitaux de Paris1
  • McMaster University1

Top Investigators

Related Conditions

  • Pompe Disease1
  • Nutrition Poor1
  • Obesity1
  • Lysosomal Storage Diseases1
  • Glycogen Storage Disease Type Ii Late Onset1

Activity Timeline