Glycogen Storage Disease Type II

Pompe Disease Registry Protocol

Clinical Study for Treatment-naïve IOPD Babies to Evaluate Efficacy and Safety of ERT With Avalglucosidase Alfa

China Post-approval Commitment (PAC) Study of Avalglucosidase Alfa in Participants With IOPD

Avalglucosidase Alfa French Post-trial Access for Participants With Pompe Disease (PTA Avalglucosidase)

A Prospective Study to Observe & Describe Clinical Outcomes of Alglucosidase Alfa Treatment in Patients ≤6 Months of Age With Infantile-onset Pompe Disease (IOPD)

A Gene Transfer Study for Late-Onset Pompe Disease (RESOLUTE)

Treatment Frequency Reduction in Pompe Disease

Nutritional Therapy in Late-onset Pompe Disease

Inspiratory Muscle Training (IMT) in Adult People With Pompe Disease

Biomarker for Glycogen Storage Diseases (BioGlycogen)

Evaluate Efficacy and Safety in Chinese Patients With Infantile-Onset Pompe Disease With One Year Alglucosidase Alfa Treatment

Higher Dose of Alglucosidase Alpha for Pompe Disease

Diet and Exercise in Pompe Disease

Fat and Sugar Metabolism During Exercise in Patients With Metabolic Myopathy

Respiratory Muscle Training in L-Onset Pompe Disease (LOPD)

Effect of Motor Development, Motor Function and Electrophysiologic Findings of IOPD Under ERT

A Prospective, Observational Study in Patients With Late-Onset Pompe Disease

High Protein and Exercise Therapy Plus Nocturnal Enteral Feeding in Juvenile-onset Pompe Disease

Safety and Efficacy of Recombinant Human Acid Alpha-Glucosidase in the Treatment of Classical Infantile Pompe Disease

An Exploratory Study of the Safety and Efficacy of Prophylactic Immunomodulatory Treatment in Myozyme-naive Cross-Reacting Immunologic Material (CRIM[-]) Patients With Infantile-Onset Pompe Disease