Glycogen Storage Disease Type I
7
2
2
2
Key Insights
Highlights
Success Rate
100% trial completion (above average)
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 50/100
0.0%
0 terminated out of 7 trials
100.0%
+13.5% vs benchmark
0%
0 trials in Phase 3/4
0%
0 of 2 completed with results
Key Signals
Data Visualizations
Phase Distribution
Trial Status
Trial Success Rate
Benchmark: 86.5%
Based on 2 completed trials
Clinical Trials (7)
Accuracy of Home Lactate Meter and Accu-chek Glucometer in Patients With Glycogen Storage Disease
Dietary Treatment Strategies and Metabolic Control in Glycogen Storage Disease Type I
Early Check: Expanded Screening in Newborns
The Use of Uncooked Sweet Manioc Starch to Treat Hepatic Glycogen Storage Diseases
Biomarker for Glycogen Storage Diseases (BioGlycogen)
Anaplerotic Therapy Using Triheptanoin for Patients With Glycogen Storage Disease Type I
Safety, Efficacy Evaluation of Empagliflozin Administration for Neutropenia in Glycogenosis Type 1b and G6PC3 Deficiency