Condition
Gaucher's disease type I; Gaucher's disease type III
Total Trials
1
Recruiting
0
Active
0
Completed
1
Key Insights
Highlights
Treatment Research
3 treatments under study, led by Imiglucerase Gz437843
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 30/100
Termination Rate
0.0%
0 terminated out of 1 trials
Late-Stage Pipeline
100%
1 trials in Phase 3/4
Results Transparency
0%
0 of 1 completed with results
Key Signals
Data Visualizations
Phase Distribution
1Total
Phase 3 (1)
Trial Status
Completed1
Clinical Trials (1)
Showing 1 of 1 trials
Showing all 1 trials
Research Network
Common Treatments
- Imiglucerase Gz4378431
- Eliglustat Gz3856601
- Eliglustat Tartrate1
Active Sponsors
- Sanofi1
- Genzyme Corp.1
Related Conditions
- Gauchers Disease Type I1
- Gauchers Disease Type Iii1