Galactosemia
4
2
2
1
Key Insights
Highlights
Success Rate
100% trial completion (above average)
Treatment Research
1 treatments under study, led by Follitropin And Lutropin
Research Leaders
6 sponsors active, led by Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)
Related Conditions
Often studied with 8 related conditions
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 50/100
0.0%
0 terminated out of 4 trials
100.0%
+13.4% vs benchmark
0%
0 trials in Phase 3/4
0%
0 of 1 completed with results
Key Signals
Data Visualizations
Phase Distribution
Trial Status
Trial Success Rate
Benchmark: 86.6%
Based on 1 completed trials
Clinical Trials (4)
Gonadal Tissue Freezing for Fertility Preservation in Individuals at Risk for Ovarian Dysfunction, Premature Ovarian Insufficiency and Clinically Indicated Gonadectomy
Gonadic Function and Pubertal Development in Female Patients With Classic Galactosemia
The Early History of Universal Screening for Metabolic Disorders
Inactive FSH in Galactosemia
Research Network
Common Treatments
- Follitropin And Lutropin1
Active Sponsors
- Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)1
- IRCCS Azienda Ospedaliero-Universitaria di Bologna1
- Maastricht University Medical Center1
- The Dutch Galactosemia Society1
- University of Miami1
Top Investigators
Maastricht University Hospital
University of Miami
Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)
Related Conditions
- Phenylketonuria1
- Postmenarcheal Adolescents1
- Variations In Sex Characteristics1
- Differences In Sex Development1
- Turner Syndrome1