Friedreich's Ataxia
28
3
3
22
Key Insights
Highlights
Success Rate
96% trial completion (above average)
Published Results
11 trials with published results (39%)
Clinical Risk Assessment
Based on trial outcomes
Low Risk
Score: 17/100
3.6%
1 terminated out of 28 trials
95.7%
+9.1% vs benchmark
32%
9 trials in Phase 3/4
50%
11 of 22 completed with results
Key Signals
Data Visualizations
Phase Distribution
Trial Status
Trial Success Rate
Benchmark: 86.5%
Based on 22 completed trials
Clinical Trials (28)
Cardiac Output and Fatigue in Friedreich's Ataxia
Patient Registry of the European Friedreich's Ataxia Consortium for Translational Studies (EFACTS)
Biomarkers in Friedreich's Ataxia
Characterization of the Cardiac Phenotype of Friedreich's Ataxia (FRDA)
Electroencephalogram in Patients With Friedreich's Ataxia for the Study of the Structural and Functional Connectome.
Safety, Tolerability and Efficacy of ACTIMMUNE® Dose Escalation in Friedreich's Ataxia Study
Safety, Tolerability and Efficacy of ACTIMMUNE® Dose Escalation in Friedreich's Ataxia
Long-Term Safety Extension Study of ACTIMMUNE® (Interferon γ-1b) in Children and Young Adults With Friedreich's Ataxia
Study to Assess the Safety and Tolerability of Idebenone in the Treatment of Friedreich's Ataxia Patients
Study to Assess the Efficacy, Safety and Tolerability of Idebenone in the Treatment of Friedreich's Ataxia
A Study to Assess Efficacy, Long Term Safety and Tolerability of RT001 in Subjects With Friedreich's Ataxia
Preliminary Study of the Scale To Assess Ataxia and Neurologic Dysfunction (STAND)
Safety and Pharmacology Study of VP 20629 in Adults With Friedreich's Ataxia
A First in Human Study of RT001 in Patients With Friedreich's Ataxia
Safety and Efficacy of EPI-743 in Patients With Friedreich's Ataxia
(+) Epicatechin to Treat Friedreich's Ataxia
A Study to Characterize the Cardiac Phenotype of Individuals With Friedreich's Ataxia (CARFA Study)
Safety Study of Carbamylated Erythropoietin to Treat Patients With the Neurodegenerative Disorder Friedreich's Ataxia
EPI-743 in Friedreich's Ataxia Point Mutations
A Study of Efficacy, Safety and Tolerability of Idebenone in the Treatment of Friedreich's Ataxia (FRDA) Patients