Fanconi Anemia
73
11
14
36
Key Insights
Highlights
Success Rate
75% trial completion
Published Results
17 trials with published results (23%)
Clinical Risk Assessment
Based on trial outcomes
High Risk
Score: 59/100
16.4%
12 terminated out of 73 trials
75.0%
-11.5% vs benchmark
1%
1 trials in Phase 3/4
47%
17 of 36 completed with results
Key Signals
Data Visualizations
Phase Distribution
Trial Status
Trial Success Rate
Benchmark: 86.5%
Based on 36 completed trials
Clinical Trials (73)
Clinical Genetics Branch Eligibility Screening Survey
Experience and Management of Cancer Screening-Related Anxiety in Fanconi Anemia
Familial Investigations of Childhood Cancer Predisposition
Quercetin Chemoprevention for Squamous Cell Carcinoma in Patients With Fanconi Anemia
Cancer in Inherited Bone Marrow Failure Syndromes
Long-Term Follow-up: Phase I/II Clinical Study to Evaluate the Safety and Efficacy of the Infusion of RP-L102
Long-Term Follow-up of Subjects With Fanconi Anaemia Subtype A Treated With ex Vivo Gene Therapy
Defining the Natural History of Squamous Cell Carcinoma in Fanconi Anemia
Widefield Fluorescence and Reflectance Imaging Systems and Oral Tissue Samples in Monitoring Participants at Risk for Developing Oral Cancer
Prenatal Transplantation for Fetuses With Fanconi Anemia
Expanded Access to CD34+ Selection Utilizing Miltenyi CliniMACS Prodigy® for Patients Receiving Peripheral Blood Stem Cell Transplantations and Stem Cell Boosts
Alpha/Beta TCD HCT in Patients With Inherited BMF Disorders
Depleted Donor Stem Cell Transplant in Children and Adults With Fanconi Anemia After Being Conditioned With a Regimen Containing Briquilimab
Regenerative Medicine to Restore Hematopoiesis and Immune Function in Immunodeficiencies and Inherited Bone Marrow Failures
HSCT for Patients With Fanconi Anemia Using Risk-Adjusted Chemotherapy
Investigation of the Genetics of Hematologic Diseases
Mobilization and Collection of Peripheral Blood Stem Cells in Patients With Fanconi Anemia Using G-CSF and Plerixafor
Eltrombopag for People With Fanconi Anemia
Role of Acetaldehyde in the Development of Oral Cancer
Baby Detect : Genomic Newborn Screening