Duchenne Muscular Dystrophy (DMD)
53
12
17
14
Key Insights
Highlights
Success Rate
78% trial completion
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 49/100
7.5%
4 terminated out of 53 trials
77.8%
-8.7% vs benchmark
4%
2 trials in Phase 3/4
50%
7 of 14 completed with results
Key Signals
Data Visualizations
Phase Distribution
Trial Status
Trial Success Rate
Benchmark: 86.5%
Based on 14 completed trials
Clinical Trials (53)
Gut Peptides and Bone Remodeling in Children With Neuromuscular Disorders
Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders
A Trial to Investigate the Safety and Pharmacokinetics of GRT6019 in Healthy Male Participants
Urinary Titin Biomarker in DMD
Invasive Home Ventilation in Denmark
A Study to Evaluate the Safety and Tolerability of Rituxan in Duchenne Muscular Dystrophy
Twice Weekly Steroids and Exercise as Therapy for DMD
A Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon 44 Skipping to Evaluate the Safety and Efficacy of ENTR-601-44
A Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon 45 Skipping to Evaluate the Safety and Efficacy of ENTR-601-45
Duchenne Muscular Dystrophy and the Viscoelastic Properties of Upper Limb Muscles
Relation Between Muscle Architecture and Functional Ability in Children With Duchenne Muscular Dystrophy
A Remote Study Using Technology to Assess Outcomes in DMD
A Trial to Investigate Safety and Pharmacokinetics of GRT6019, Including Food Effect, in Healthy Male Participants
Registry for Duchenne and Becker Muscular Dystrophy
Factors Influencing Physical Activity Levels in Children With Duchenne Muscular Dystrophy: An ICF-CY-Based Study
DMD and Gamified Physiotherapy
The Effect of Dual-tasking Program on Cognitive and Physical Functions and Independence in Activities of Daily Living in Children With Duchenne Muscular Dystrophy: A Single-blind Randomized Controlled Trial
Self-Efficacy Enhancement Using a Multicomponent Support Group for Caregivers of Children With DMD/SMA
A Study to Evaluate the Safety and Tolerability of RAG-18 in Pediatric Patients With Duchenne Muscular Dystrophy
Virtual Reality and Whole Body Vibration on Muscle Strength and Balance in Children With DMD