Condition
Duchenne / Becker Muscular Dystrophy
Total Trials
4
Recruiting
1
Active
1
Completed
1
Success Rate
100.0%+13% vs avg
Key Insights
Highlights
Success Rate
100% trial completion (above average)
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 50/100
Termination Rate
0.0%
0 terminated out of 4 trials
Success Rate
100.0%
+13.5% vs benchmark
Late-Stage Pipeline
0%
0 trials in Phase 3/4
Results Transparency
0%
0 of 1 completed with results
Key Signals
100% success
Data Visualizations
Phase Distribution
2Total
Not Applicable (2)
Trial Status
Not Yet Recruiting2
Recruiting1
Completed1
Trial Success Rate
100.0%
Benchmark: 86.5%
Based on 1 completed trials
Clinical Trials (4)
Showing 4 of 4 trials
NCT07415837Not ApplicableRecruitingPrimary
Evaluation of the Role of miR-1 in the Pathogenesis and as a Biomarker in Muscular Dystrophies and Congenital Myopathies
NCT07101185Not ApplicableNot Yet RecruitingPrimary
Transition to Adulthood in People With Muscular Dystrophy
NCT02470962CompletedPrimary
Cardiac Involvement in Patients With Duchenne/Becker Muscular Dystrophy
NCT06874166Not Yet RecruitingPrimary
Social Cognition in Dystrophinopathies and Neurodevelopmental Disorders
Showing all 4 trials