DMD

Phase 2 Study of SAT-3247 in Pediatric Ambulatory Patients

Ph2 Open-label Study of AOC 1044 in Duchenne Muscular Dystrophy Participants With Mutations Amenable to Exon44 Skipping

A Phase 3 Study to Evaluate the Safety and Efficacy of AOC 1044 (Also Referred to as Delpacibart Zotadirsen) in Participants With DMD With Gene Mutations Amenable to Exon 44 Skipping

Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO)

Vasodilator and Exercise Study for DMD (VASO-REx)

NS-089/NCNP-02-201 in Boys With Duchenne Muscular Dystrophy (DMD)

Swiss Registry for Neuromuscular Disorders

A Clinical Study to Evaluate the Safety, Tolerability, and Efficacy of BBM-D101 in the Treatment of Duchenne Muscular Dystrophy.

ML-Based Multi-Sensor Fall Risk Screening in DMD

Defining Outcome Measures for Behavioural and Emotional Problems in Dystrophinopathies

Tissue Repository Providing Annotated Biospecimens for Approved Investigator-directed Biomedical Research Initiatives

Multi-center Clinical Study on the Diagnosis and Treatment Management of Rare Neurological Disease in Children

Constipation and Gut Transit in DMD Patients

The Expanded Access Use of Viltolarsen in Duchenne Muscular Dystrophy With Confirmed Exon 53 Amenable Mutation