DMD
12
8
9
1
Key Insights
Highlights
Success Rate
100% trial completion (above average)
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 50/100
0.0%
0 terminated out of 12 trials
100.0%
+13.5% vs benchmark
0%
0 trials in Phase 3/4
0%
0 of 1 completed with results
Key Signals
Data Visualizations
Phase Distribution
Trial Status
Trial Success Rate
Benchmark: 86.5%
Based on 1 completed trials
Clinical Trials (12)
Phase 2 Study of SAT-3247 in Pediatric Ambulatory Patients
NS-089/NCNP-02-201 in Boys With Duchenne Muscular Dystrophy (DMD)
Swiss Registry for Neuromuscular Disorders
A Clinical Study to Evaluate the Safety, Tolerability, and Efficacy of BBM-D101 in the Treatment of Duchenne Muscular Dystrophy.
Vasodilator and Exercise Study for DMD (VASO-REx)
ML-Based Multi-Sensor Fall Risk Screening in DMD
Ph2 Open-label Study of AOC 1044 in Duchenne Muscular Dystrophy Participants With Mutations Amenable to Exon44 Skipping
Defining Outcome Measures for Behavioural and Emotional Problems in Dystrophinopathies
Tissue Repository Providing Annotated Biospecimens for Approved Investigator-directed Biomedical Research Initiatives
Multi-center Clinical Study on the Diagnosis and Treatment Management of Rare Neurological Disease in Children
Constipation and Gut Transit in DMD Patients
The Expanded Access Use of Viltolarsen in Duchenne Muscular Dystrophy With Confirmed Exon 53 Amenable Mutation