Key Insights

Highlights

Treatment Research

2 treatments under study, led by Skin Biopsy

Clinical Risk Assessment

Based on trial outcomes

Moderate Risk

Score: 50/100

Termination Rate

0.0%

0 terminated out of 1 trials

Late-Stage Pipeline

0%

0 trials in Phase 3/4

Results Transparency

0%

0 of 0 completed with results

Key Signals

Data Visualizations

Phase Distribution

1Total
Not Applicable (1)

Trial Status

Recruiting1

Clinical Trials (1)

Research Network

Common Treatments

  • Skin Biopsy1
  • Muscle Biopsy1

Active Sponsors

  • Institut National de la Santé Et de la Recherche Médicale, France1

Related Conditions

  • Laminopathies1
  • Lmnarelated Congenital Muscular Dystrophy1
  • Emery Dreifuss Muscular Dystrophy 21

Activity Timeline