Diamond Blackfan Anemia
16
3
3
6
Key Insights
Highlights
Success Rate
50% trial completion
Clinical Risk Assessment
Based on trial outcomes
High Risk
Score: 75/100
37.5%
6 terminated out of 16 trials
50.0%
-36.5% vs benchmark
6%
1 trials in Phase 3/4
133%
8 of 6 completed with results
Key Signals
Data Visualizations
Phase Distribution
Trial Status
Trial Success Rate
Benchmark: 86.5%
Based on 6 completed trials
Clinical Trials (16)
Cancer in Inherited Bone Marrow Failure Syndromes
Mobilization of CD34+ Peripheral Blood Stem Cells in Patients With Diamond Blackfan Anemia Syndrome (DBAS)
Bone Marrow and Kidney Transplant for Patients With Chronic Kidney Disease and Blood Disorders
Baby Detect : Genomic Newborn Screening
AlloSCT for Malignant and Non-malignant Hematologic Diseases Utilizing Alpha/Beta T Cell and CD19+ B Cell Depletion
Hematopoietic Stem Cell Transplant for High Risk Hemoglobinopathies
Safety Study of Gene Modified Donor T-cells Following TCRαβ+ Depleted Stem Cell Transplant
Long Term Follow-up Study for Patients Enrolled on the BP-004 Clinical Study
Conditioning Regimen for Allogeneic Hematopoietic Stem-Cell Transplantation
Safety and Efficacy Study of Sotatercept in Adults With Transfusion Dependent Diamond Blackfan Anemia
The Use of Trifluoperazine in Transfusion Dependent DBA
Pilot Phase I/II Study of Amino Acid Leucine in Treatment of Patients With Transfusion-Dependent Diamond Blackfan Anemia
A Study to Determine Whether Therapy With Daclizumab Will Benefit Patients With Bone Marrow Failure
L-leucine in Diamond Blackfan Anemia Patients
Expanded Access of Deferasirox to Patients With Congenital Disorders of Red Blood Cells and Chronic Iron Overload
Mobilization of Stem Cells With G-CSF for Collection From Patients With Diamond-Blackfan Anemia