Condition
Deficiency Disease
Total Trials
3
Recruiting
0
Active
0
Completed
2
Success Rate
100.0%+13% vs avg
Key Insights
Highlights
Success Rate
100% trial completion (above average)
Treatment Research
2 treatments under study, led by Echography
Related Conditions
Often studied with 5 related conditions
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 50/100
Termination Rate
0.0%
0 terminated out of 3 trials
Success Rate
100.0%
+13.4% vs benchmark
Late-Stage Pipeline
0%
0 trials in Phase 3/4
Results Transparency
0%
0 of 2 completed with results
Key Signals
100% success
Data Visualizations
Phase Distribution
2Total
Not Applicable (1)
Phase 2 (1)
Trial Status
Completed2
Withdrawn1
Trial Success Rate
100.0%
Benchmark: 86.6%
Based on 2 completed trials
Clinical Trials (3)
Research Network
Common Treatments
- Echography1
- Lithium Gluconate Drug Glyceryl Triacetate Gta Drug1
Active Sponsors
- Assistance Publique - Hôpitaux de Paris2
- European Leukodystrophy Association1
- Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)1
Top Investigators
Assistance Publique - Hôpitaux de Paris
Assistance Publique - Hôpitaux de Paris
Assistance Publique - Hôpitaux de Paris
Related Conditions
- Healthy1
- Canavan Disease1
- Aspartoacylase1
- Leukodystrophy Spongiform1
- Infantile1