Key Insights

Highlights

Success Rate

100% trial completion (above average)

Treatment Research

2 treatments under study, led by Echography

Related Conditions

Often studied with 5 related conditions

Clinical Risk Assessment

Based on trial outcomes

Moderate Risk

Score: 50/100

Termination Rate

0.0%

0 terminated out of 3 trials

Success Rate

100.0%

+13.4% vs benchmark

Late-Stage Pipeline

0%

0 trials in Phase 3/4

Results Transparency

0%

0 of 2 completed with results

Key Signals

100% success

Data Visualizations

Phase Distribution

2Total
Not Applicable (1)
Phase 2 (1)

Trial Status

Completed2
Withdrawn1

Trial Success Rate

100.0%

Benchmark: 86.6%

Based on 2 completed trials

Clinical Trials (3)

Research Network

Common Treatments

  • Echography1
  • Lithium Gluconate Drug Glyceryl Triacetate Gta Drug1

Active Sponsors

  • Assistance Publique - Hôpitaux de Paris2
  • European Leukodystrophy Association1
  • Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)1

Top Investigators

Related Conditions

  • Healthy1
  • Canavan Disease1
  • Aspartoacylase1
  • Leukodystrophy Spongiform1
  • Infantile1

Activity Timeline