Condition
Danon Disease
Total Trials
7
Recruiting
4
Active
4
Completed
1
Success Rate
100.0%+13% vs avg
Key Insights
Highlights
Success Rate
100% trial completion (above average)
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 50/100
Termination Rate
0.0%
0 terminated out of 7 trials
Success Rate
100.0%
+13.5% vs benchmark
Late-Stage Pipeline
0%
0 trials in Phase 3/4
Results Transparency
0%
0 of 1 completed with results
Key Signals
100% success
Data Visualizations
Phase Distribution
2Total
P 1 (1)
P 2 (1)
Trial Status
Recruiting4
Unknown2
Completed1
Trial Success Rate
100.0%
Benchmark: 86.5%
Based on 1 completed trials
Clinical Trials (7)
Showing 7 of 7 trials
NCT06214507RecruitingPrimary
Danon Disease Natural History Study
NCT06092034Phase 2RecruitingPrimary
A Gene Therapy Study of RP-A501 in Male Patients With Danon Disease
NCT07336394RecruitingPrimary
Precision Diagnosis and Risk Stratification of Rare Cardiomyopathies Based on Novel Cardiac Magnetic Resonance Techniques
NCT06795152Recruiting
Rare Glycogen Storage Diseases Natural History Study
NCT05548855CompletedPrimary
Natural History of Danon Disease
NCT03882437Phase 1UnknownPrimary
Gene Therapy for Male Patients With Danon Disease (DD) Using RP-A501; AAV9.LAMP2B
NCT03766386UnknownPrimary
The Natural History of Danon Disease
Showing all 7 trials