Key Insights

Highlights

Success Rate

100% trial completion (above average)

Treatment Research

11 treatments under study, led by Questionnaire

Research Leaders

9 sponsors active, led by Novartis Pharmaceuticals

Related Conditions

Often studied with 9 related conditions

Clinical Risk Assessment

Based on trial outcomes

Moderate Risk

Score: 40/100

Termination Rate

0.0%

0 terminated out of 8 trials

Success Rate

100.0%

+13.4% vs benchmark

Late-Stage Pipeline

13%

1 trials in Phase 3/4

Results Transparency

0%

0 of 5 completed with results

Key Signals

100% success

Data Visualizations

Phase Distribution

6Total
Not Applicable (1)
Phase 1 (2)
Phase 2 (2)
Phase 3 (1)

Trial Status

Completed5
Recruiting1
Not Yet Recruiting1
Unknown1

Trial Success Rate

100.0%

Benchmark: 86.6%

Based on 5 completed trials

Clinical Trials (8)

Research Network

Common Treatments

  • Questionnaire1
  • Vtx27351
  • Blood Sampling1
  • Izd3341
  • Placebos1

Active Sponsors

  • Novartis Pharmaceuticals1
  • University Hospital, Lille1
  • NodThera Limited1
  • Zydus Lifesciences Limited1
  • Zomagen Biosciences Ltd.1

Top Investigators

Related Conditions

  • Mkd1
  • Traps1
  • Mucklewells Syndrome1
  • Autoinflammatory Disease1
  • Fmf1

Activity Timeline