Condition
Cri-du-Chat Syndrome
Total Trials
2
Recruiting
1
Active
1
Completed
1
Success Rate
100.0%+13% vs avg
Key Insights
Highlights
Success Rate
100% trial completion (above average)
Treatment Research
1 treatments under study, led by Pace Program
Research Leaders
7 sponsors active, led by National Institute on Aging (NIA)
Related Conditions
Often studied with 20 related conditions
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 50/100
Termination Rate
0.0%
0 terminated out of 2 trials
Success Rate
100.0%
+13.4% vs benchmark
Late-Stage Pipeline
0%
0 trials in Phase 3/4
Results Transparency
0%
0 of 1 completed with results
Key Signals
100% success
Data Visualizations
Phase Distribution
1Total
Not Applicable (1)
Trial Status
Recruiting1
Completed1
Trial Success Rate
100.0%
Benchmark: 86.6%
Based on 1 completed trials
Clinical Trials (2)
Showing 2 of 2 trials
NCT06740162Not ApplicableRecruiting
Physical Activity and Community EmPOWERment Project
NCT02381457Completed
SNP-based Microdeletion and Aneuploidy RegisTry (SMART)
Showing all 2 trials
Research Network
Common Treatments
- Pace Program1
Active Sponsors
- National Institute on Aging (NIA)1
- Children's Hospital of Philadelphia1
- University of North Carolina, Chapel Hill1
- University of California, San Francisco1
- George Washington University1
Top Investigators
University of California, San Francisco
Montefiore Medical Center
University of North Carolina, Chapel Hill
Related Conditions
- Praderwilli Syndrome2
- Trisomy 13 Syndrome1
- Fragile X Syndrome1
- Neurodevelopmental Disorders1
- Williams Syndrome1