Key Insights

Highlights

Success Rate

100% trial completion (above average)

Research Leaders

10 sponsors active, led by IRCCS National Neurological Institute "C. Mondino" Foundation

Clinical Risk Assessment

Based on trial outcomes

Moderate Risk

Score: 50/100

Termination Rate

0.0%

0 terminated out of 2 trials

Success Rate

100.0%

+13.4% vs benchmark

Late-Stage Pipeline

0%

0 trials in Phase 3/4

Results Transparency

0%

0 of 1 completed with results

Key Signals

100% success

Data Visualizations

Phase Distribution

Trial Status

Completed1
Recruiting1

Trial Success Rate

100.0%

Benchmark: 86.6%

Based on 1 completed trials

Clinical Trials (2)

Research Network

Active Sponsors

  • IRCCS National Neurological Institute "C. Mondino" Foundation1
  • Istituto Giannina Gaslini1
  • Virginia Commonwealth University1
  • A.O.U. Città della Salute e della Scienza1
  • Fondazione Serena Onlus - Centro Clinico NeMO Milano1

Top Investigators

Related Conditions

  • Chdm1
  • Congenital Myotonic Dystrophy1

Activity Timeline