Condition
CDM
Total Trials
2
Recruiting
1
Active
1
Completed
1
Success Rate
100.0%+13% vs avg
Key Insights
Highlights
Success Rate
100% trial completion (above average)
Research Leaders
10 sponsors active, led by IRCCS National Neurological Institute "C. Mondino" Foundation
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 50/100
Termination Rate
0.0%
0 terminated out of 2 trials
Success Rate
100.0%
+13.4% vs benchmark
Late-Stage Pipeline
0%
0 trials in Phase 3/4
Results Transparency
0%
0 of 1 completed with results
Key Signals
100% success
Data Visualizations
Phase Distribution
Trial Status
Completed1
Recruiting1
Trial Success Rate
100.0%
Benchmark: 86.6%
Based on 1 completed trials
Clinical Trials (2)
Research Network
Active Sponsors
- IRCCS National Neurological Institute "C. Mondino" Foundation1
- Istituto Giannina Gaslini1
- Virginia Commonwealth University1
- A.O.U. Città della Salute e della Scienza1
- Fondazione Serena Onlus - Centro Clinico NeMO Milano1
Top Investigators
Virginia Commonwealth University
Related Conditions
- Chdm1
- Congenital Myotonic Dystrophy1