Condition
Bone Marrow Failure Disorders
Total Trials
4
Recruiting
1
Active
1
Completed
1
Success Rate
100.0%+13% vs avg
Key Insights
Highlights
Success Rate
100% trial completion (above average)
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 50/100
Termination Rate
0.0%
0 terminated out of 4 trials
Success Rate
100.0%
+13.5% vs benchmark
Late-Stage Pipeline
0%
0 trials in Phase 3/4
Results Transparency
0%
0 of 1 completed with results
Key Signals
100% success
Data Visualizations
Phase Distribution
3Total
Early P 1 (1)
P 1 (2)
Trial Status
Not Yet Recruiting1
Completed1
Recruiting1
Enrolling By Invitation1
Trial Success Rate
100.0%
Benchmark: 86.5%
Based on 1 completed trials
Clinical Trials (4)
Showing 4 of 4 trials
NCT07408583Phase 1Not Yet Recruiting
Prenatal Transplantation for Fetuses With Fanconi Anemia
NCT07102849Enrolling By InvitationPrimary
Molecular and Clinical Analysis of Bone Marrow Failure: A Secondary Research Study
NCT04478227Early Phase 1CompletedPrimary
TPO-Mimetic Use in Children for Hematopoietic Failure
NCT05794425Phase 1RecruitingPrimary
Clinical Study of UCB Combined With UC-MSCs in the Treatment of Bone Marrow Failure Disorders
Showing all 4 trials