Key Insights

Highlights

Success Rate

100% trial completion (above average)

Treatment Research

11 treatments under study, led by Cytokine Essays

Research Leaders

5 sponsors active, led by Children's Hospital of Philadelphia

Related Conditions

Often studied with 15 related conditions

Clinical Risk Assessment

Based on trial outcomes

Low Risk

Score: 25/100

Termination Rate

0.0%

0 terminated out of 4 trials

Success Rate

100.0%

+13.4% vs benchmark

Late-Stage Pipeline

0%

0 trials in Phase 3/4

Results Transparency

100%

1 of 1 completed with results

Key Signals

1 with results100% success

Data Visualizations

Phase Distribution

2Total
Phase 1/2 (1)
Phase 2 (1)

Trial Status

Recruiting2
Completed1
Not Yet Recruiting1

Trial Success Rate

100.0%

Benchmark: 86.6%

Based on 1 completed trials

Clinical Trials (4)

Research Network

Common Treatments

  • Cytokine Essays1
  • Thrombopoietin Receptor Agonist1
  • Granulocyte Colonystimulating Factor1
  • Mavorixafor1
  • Blood Sample1

Active Sponsors

  • Children's Hospital of Philadelphia1
  • University Hospital, Bordeaux1
  • Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico1
  • Ministry for Health and Solidarity, France1
  • X4 Pharmaceuticals1

Top Investigators

Related Conditions

  • Autoimmune Hemolytic Anemia2
  • Chronic Idiopathic Neutropenia2
  • Immune Thrombocytopenia2
  • Idiopathic Thrombocytopenic Purpura1
  • Autoimmune Lymphoproliferative Syndrome Alps1

Activity Timeline