Key Insights

Highlights

Related Conditions

Often studied with 11 related conditions

Clinical Risk Assessment

Based on trial outcomes

Moderate Risk

Score: 50/100

Termination Rate

0.0%

0 terminated out of 1 trials

Late-Stage Pipeline

0%

0 trials in Phase 3/4

Results Transparency

0%

0 of 0 completed with results

Key Signals

Data Visualizations

Phase Distribution

Trial Status

Recruiting1

Clinical Trials (1)

Showing 1 of 1 trials
Showing all 1 trials

Research Network

Active Sponsors

  • Clinic for Special Children1

Top Investigators

Related Conditions

  • Myopathy1
  • Genetic Muscle Disease1
  • Myopathy Hereditary1
  • Nem51
  • Recessive Hereditary Disorder Autosomal1

Activity Timeline