Condition
Amino Acid Metabolism, Inborn Errors
Total Trials
6
Recruiting
2
Active
2
Completed
2
Success Rate
66.7%-20% vs avg
Key Insights
Highlights
Success Rate
67% trial completion
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 47/100
Termination Rate
16.7%
1 terminated out of 6 trials
Success Rate
66.7%
-19.8% vs benchmark
Late-Stage Pipeline
0%
0 trials in Phase 3/4
Results Transparency
100%
2 of 2 completed with results
Key Signals
2 with results67% success
Data Visualizations
Phase Distribution
5Total
Not Applicable (1)
P 1 (1)
P 2 (3)
Trial Status
Completed2
Recruiting2
Unknown1
Terminated1
Trial Success Rate
66.7%
Benchmark: 86.5%
Based on 2 completed trials
Clinical Trials (6)
Showing 6 of 6 trials
NCT06337864Not ApplicableRecruiting
Effect of Large Neutral Amino Acids in Adults With Classical Phenylketonuria
NCT00237315Recruiting
Longitudinal Study of Urea Cycle Disorders
NCT01141075Phase 2TerminatedPrimary
Ataluren for Nonsense Mutation Methylmalonic Acidemia
NCT00345605Phase 2Completed
Arginine and Buphenyl in Patients With Argininosuccinic Aciduria (ASA), a Urea Cycle Disorder
NCT00004767Phase 2CompletedPrimary
Phase II Study of Sodium Phenylbutyrate, Sodium Benzoate, Sodium Phenylacetate, and Dietary Intervention for Urea Cycle Disorders
NCT00004307Phase 1UnknownPrimary
Study of Treatment and Metabolism in Patients With Urea Cycle Disorders
Showing all 6 trials