Alkaptonuria
9
1
1
5
Key Insights
Highlights
Success Rate
100% trial completion (above average)
Clinical Risk Assessment
Based on trial outcomes
Low Risk
Score: 27/100
0.0%
0 terminated out of 9 trials
100.0%
+13.5% vs benchmark
11%
1 trials in Phase 3/4
40%
2 of 5 completed with results
Key Signals
Data Visualizations
Phase Distribution
Trial Status
Trial Success Rate
Benchmark: 86.5%
Based on 5 completed trials
Clinical Trials (9)
Study of Alkaptonuria
Questionnaire Follow=up Study Sonia 2
Acceptability/Tolerance of Protein Substitutes in Tablet Form for the Dietary Management of Rare Aminoacidopathies
Evaluation of TYR Sphere
Long-Term Study of Nitisinone to Treat Alkaptonuria
Nitisinone (NTBC) In Different Age Groups Of Patients With Alkaptonuria
Individualised Gait Modification Strategies in Alkaptonuria Patients
Suitability of Nitisinone in Alkaptonuria 2
Dose Response Study of Nitisinone in Alkaptonuria