Adrenoleukodystrophy
25
5
6
12
Key Insights
Highlights
Success Rate
80% trial completion
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 49/100
12.0%
3 terminated out of 25 trials
80.0%
-6.5% vs benchmark
12%
3 trials in Phase 3/4
50%
6 of 12 completed with results
Key Signals
Data Visualizations
Phase Distribution
Trial Status
Trial Success Rate
Benchmark: 86.5%
Based on 12 completed trials
Clinical Trials (25)
Treating Leg Symptoms in Women With X-linked Adrenoleukodystrophy
LeukoSEQ: Whole Genome Sequencing as a First-Line Diagnostic Tool for Leukodystrophies
The Myelin Disorders Biorepository Project
Modeling Macrophages Activation Pattern in X-linked Adrenoleukodystrophy, Metachromatic Leukodystrophy and Adult Onset Leukoencephalopathy With Axonal Spheroids and Pigmented Glia
UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells
Baby Detect : Genomic Newborn Screening
Adrenoleukodystrophy National Registry Study
A Clinical Study to Evaluate the Efficacy and Safety of MIN-102 (IMP) in Male AMN Patients.
Precision Exercise in Children With Malignant Hemopathies
Compassionate Treatment of Patients With Inborn Errors of Bile Acid Metabolism With Cholic Acid
Conditioning Regimen for Allogeneic Hematopoietic Stem-Cell Transplantation
Human Placental-Derived Stem Cell Transplantation
Plasma Exchange With Albumin in AMN Patients
Autologous Hematopoietic Stem Cell Gene Therapy for Metachromatic Leukodystrophy and Adrenoleukodystrophy
Effect of Glycerol Trierucate on Clinical Course of Adrenoleukodystrophy
HSCT for High Risk Inherited Inborn Errors
Newborn Screening for Adrenoleukodystrophy
Early Diagnosis Of Childhood Cerebral ALD
Stem Cell Transplant for Inborn Errors of Metabolism
MD1003-AMN MD1003 in Adrenomyeloneuropathy