Key Insights

Highlights

Treatment Research

6 treatments under study, led by Obtaining Dry Blood Spots From Highrisk Childrens Aged 8 18 Years

Related Conditions

Often studied with 20 related conditions

Clinical Risk Assessment

Based on trial outcomes

Moderate Risk

Score: 50/100

Termination Rate

0.0%

0 terminated out of 1 trials

Late-Stage Pipeline

0%

0 trials in Phase 3/4

Results Transparency

0%

0 of 0 completed with results

Key Signals

Data Visualizations

Phase Distribution

Trial Status

Unknown1

Clinical Trials (1)

Research Network

Common Treatments

  • Obtaining Dry Blood Spots From Highrisk Childrens Aged 8 18 Years1
  • Obtaining Dry Blood Spots From Healthy Newborns Aged 17 Days1
  • Obtaining Dry Blood Spots From Highrisk Newborns Aged 17 Days1
  • Obtaining Dry Blood Spots From Healthy Children Aged 8 Days 7 Years1
  • Obtaining Dry Blood Spots From Highrisk Childrens Aged 8 Days 7 Years1

Active Sponsors

  • West Kazakhstan Medical University1

Top Investigators

Related Conditions

  • Longchain 3hydroxyacylcoa Dehydrogenase Deficiency1
  • Mediumchain Acylcoa Dehydrogenase Deficiency1
  • Betaketothiolase Deficiency1
  • Very Longchain Acylcoa Dehydrogenase Deficiency1
  • Isovaleric Acidemia1

Activity Timeline